Genetics
News, opinions and meeting coverage in genetics.
Latest in Genetics
Arimoclomol (Miplyffa) greenlit for ultra-rare genetic disorder
Findings "shift the dial more in favor of an animal origin," said one expert
Health news and commentary gathered by MedPage Today staff
Benefits seen in patients with and without a genetic diagnosis
Health news and commentary gathered by MedPage Today staff
Benefits seen in patients with and without a genetic diagnosis
More in Genetics
Phase III trial falls short of efficacy target, but positive signal emerges in younger kids
This is the second time the drug has been submitted to the FDA for Niemann-Pick disease type C
In randomized study, guided site-specific therapy improved PFS versus empirical chemotherapy
Studies show 90% reduction in intravitreal treatment burden, durable effect on vision, anatomy
U.S. clinics market oligonucleotide therapy for a wide range of conditions, without much evidence
Phase II study found brigatinib exceeded historical control by shrinking 10% of targeted tumors