Genetics
Genetics
More in Genetics
Phase III trial falls short of efficacy target, but positive signal emerges in younger kids
Aug 23, 2024
This is the second time the drug has been submitted to the FDA for Niemann-Pick disease type C
Aug 01, 2024
Studies show 90% reduction in intravitreal treatment burden, durable effect on vision, anatomy
Jul 18, 2024
U.S. clinics market oligonucleotide therapy for a wide range of conditions, without much evidence
Jul 05, 2024